 @article{camelo_mendonça_moreno_polido_carvalho_teixeira_hayashi_brito_matsui junior_zanoteli_2026, title={Real-world 12-month outcomes of Risdiplam in spinal muscular atrophy types 2 and 3: A Brazilian cohort}, volume={81}, ISSN={1807-5932}, url={https://doi.org/10.1016/j.clinsp.2026.101027}, DOI={10.1016/j.clinsp.2026.101027}, journal={Clinics}, publisher={Faculdade de Medicina / USP}, author={Camelo, Clara Gontijo and Mendonça, Rodrigo Holanda and Moreno, Cristiane Araujo Martins and Polido, Graziela Jorge and Carvalho, Eduardo Vital de and Teixeira, Weverton Carlos da Silva and Hayashi, Daniel Shoji and Brito, Joemir Jabson da Conceição and Matsui Junior, Ciro and Zanoteli, Edmar}, year={2026}, pages={101027} }