TY  - JOUR 
T1  - Results From a 12-Month Open-Label Phase 1/2 Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease
JO  - Journal of Inborn Errors of Metabolism and Screening
A1  - Tantawy, Azza A. G.
A1  - El-Beshlawy, Amal
A1  - Marzouk, Iman
A1  - Bavdekar, Ashish
A1  - Qin, Yulin
A1  - Mellgard, Björn
A1  - Turkia, Hadhami Ben
SN  - 2326-4594
UL  - 10.1177/2326409818765564
VL  - 6 
Y1  - 2018
PB  - Brasil 
ER  -