@article{tantawy_el-beshlawy_marzouk_bavdekar_qin_mellgard_turkia_2018,  title={Results From a 12-Month Open-Label Phase 1/2 Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease},  volume={6},  ISSN={2326-4594},  url={https://doi.org/10.1177/2326409818765564},  DOI={10.1177/2326409818765564},  journal={Journal of Inborn Errors of Metabolism and Screening},  publisher={Latin American Society Inborn Errors and Neonatal Screening (SLEIMPN); Instituto Genética para Todos (IGPT)},  author={Tantawy, Azza A. G. and El-Beshlawy, Amal and Marzouk, Iman and Bavdekar, Ashish and Qin, Yulin and Mellgard, Björn and Turkia, Hadhami Ben},  year={2018} }